World's youngest patient receives groundbreaking gene therapy in Cincinnati
World's youngest patient receives groundbreaking gene therapy in Cincinnati,Further delineation of the rare GDACCF (global developmental delay, absent or hypoplastic corpus callosum, dysmorphic facies syndrome): genotype and phenotype of 22 patients with ZNF148 mutations | Journal of Medical Genetics,Infected blood scandal: Children were used as 'guinea pigs' in clinical trials